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HK1262955B - 用於治疗dravet综合征的反义寡聚体 - Google Patents

用於治疗dravet综合征的反义寡聚体

Info

Publication number
HK1262955B
HK1262955B HK19122867.5A HK19122867A HK1262955B HK 1262955 B HK1262955 B HK 1262955B HK 19122867 A HK19122867 A HK 19122867A HK 1262955 B HK1262955 B HK 1262955B
Authority
HK
Hong Kong
Prior art keywords
mrna
scn1a
intron
protein
aso
Prior art date
Application number
HK19122867.5A
Other languages
German (de)
English (en)
French (fr)
Other versions
HK1262955A1 (zh
Inventor
Isabel AZNAREZ
Huw M. Nash
Adrian Krainer
Original Assignee
Cold Spring Harbor Laboratory
Stoke Therapeutics, Inc.
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Cold Spring Harbor Laboratory, Stoke Therapeutics, Inc. filed Critical Cold Spring Harbor Laboratory
Publication of HK1262955A1 publication Critical patent/HK1262955A1/zh
Publication of HK1262955B publication Critical patent/HK1262955B/zh

Links

HK19122867.5A 2015-12-14 2016-12-14 用於治疗dravet综合征的反义寡聚体 HK1262955B (zh)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
US201562267251 2015-12-14

Publications (2)

Publication Number Publication Date
HK1262955A1 HK1262955A1 (zh) 2020-01-24
HK1262955B true HK1262955B (zh) 2022-02-04

Family

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