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HK1262960B - 用於治疗视网膜色素变性13的组合物 - Google Patents

用於治疗视网膜色素变性13的组合物

Info

Publication number
HK1262960B
HK1262960B HK19122873.3A HK19122873A HK1262960B HK 1262960 B HK1262960 B HK 1262960B HK 19122873 A HK19122873 A HK 19122873A HK 1262960 B HK1262960 B HK 1262960B
Authority
HK
Hong Kong
Prior art keywords
artificial sequence
rna
cases
synthetic oligonucleotide
mrna
Prior art date
Application number
HK19122873.3A
Other languages
German (de)
English (en)
French (fr)
Other versions
HK1262960A1 (zh
Inventor
Isabel AZNAREZ
Huw M. Nash
Adrian Krainer
Original Assignee
Cold Spring Harbor Laboratory
Stoke Therapeutics, Inc.
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Cold Spring Harbor Laboratory, Stoke Therapeutics, Inc. filed Critical Cold Spring Harbor Laboratory
Publication of HK1262960A1 publication Critical patent/HK1262960A1/zh
Publication of HK1262960B publication Critical patent/HK1262960B/zh

Links

HK19122873.3A 2015-12-14 2016-12-14 用於治疗视网膜色素变性13的组合物 HK1262960B (zh)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
US201562267261 2015-12-14

Publications (2)

Publication Number Publication Date
HK1262960A1 HK1262960A1 (zh) 2020-01-24
HK1262960B true HK1262960B (zh) 2022-04-14

Family

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