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MX2022003585A - Metodos para tratar hiperfenilalaninemia. - Google Patents

Metodos para tratar hiperfenilalaninemia.

Info

Publication number
MX2022003585A
MX2022003585A MX2022003585A MX2022003585A MX2022003585A MX 2022003585 A MX2022003585 A MX 2022003585A MX 2022003585 A MX2022003585 A MX 2022003585A MX 2022003585 A MX2022003585 A MX 2022003585A MX 2022003585 A MX2022003585 A MX 2022003585A
Authority
MX
Mexico
Prior art keywords
methods
hyperphenylalaninemia
treat
sepiapterin
administration
Prior art date
Application number
MX2022003585A
Other languages
English (en)
Inventor
Niel Smith
Original Assignee
Ptc Therapeutics Mp Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Ptc Therapeutics Mp Inc filed Critical Ptc Therapeutics Mp Inc
Publication of MX2022003585A publication Critical patent/MX2022003585A/es

Links

Classifications

    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P3/00Drugs for disorders of the metabolism
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00Medicinal preparations containing organic active ingredients
    • A61K31/33Heterocyclic compounds
    • A61K31/395Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/495Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with two or more nitrogen atoms as the only ring heteroatoms, e.g. piperazine or tetrazines
    • A61K31/505Pyrimidines; Hydrogenated pyrimidines, e.g. trimethoprim
    • A61K31/519Pyrimidines; Hydrogenated pyrimidines, e.g. trimethoprim ortho- or peri-condensed with heterocyclic rings
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/0087Galenical forms not covered by A61K9/02 - A61K9/7023
    • A61K9/0095Drinks; Beverages; Syrups; Compositions for reconstitution thereof, e.g. powders or tablets to be dispersed in a glass of water; Veterinary drenches

Landscapes

  • Health & Medical Sciences (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Veterinary Medicine (AREA)
  • Public Health (AREA)
  • General Health & Medical Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Animal Behavior & Ethology (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Medicinal Chemistry (AREA)
  • Epidemiology (AREA)
  • Obesity (AREA)
  • Organic Chemistry (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • General Chemical & Material Sciences (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Hematology (AREA)
  • Diabetes (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Engineering & Computer Science (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
  • Medicinal Preparation (AREA)

Abstract

La invención presenta métodos para reducir la concentración de fenilalanina en sangre en un sujeto por la administración de sepiapterina, o una sal farmacéuticamente aceptable de la misma.
MX2022003585A 2019-09-25 2020-09-25 Metodos para tratar hiperfenilalaninemia. MX2022003585A (es)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201962905720P 2019-09-25 2019-09-25
PCT/US2020/052871 WO2021062264A1 (en) 2019-09-25 2020-09-25 Methods for treating hyperphenylalaninemia

Publications (1)

Publication Number Publication Date
MX2022003585A true MX2022003585A (es) 2022-04-19

Family

ID=72827023

Family Applications (1)

Application Number Title Priority Date Filing Date
MX2022003585A MX2022003585A (es) 2019-09-25 2020-09-25 Metodos para tratar hiperfenilalaninemia.

Country Status (23)

Country Link
US (1) US20220362249A1 (es)
EP (1) EP4034122B1 (es)
JP (2) JP7661315B2 (es)
KR (1) KR20220070477A (es)
CN (1) CN114650825A (es)
AU (1) AU2020353676A1 (es)
BR (1) BR112022003719A2 (es)
CA (1) CA3150003A1 (es)
DK (1) DK4034122T3 (es)
ES (1) ES3041002T3 (es)
FI (1) FI4034122T3 (es)
HR (1) HRP20251268T1 (es)
HU (1) HUE073483T2 (es)
IL (1) IL291565A (es)
JO (1) JOP20220042A1 (es)
LT (1) LT4034122T (es)
MX (1) MX2022003585A (es)
PL (1) PL4034122T3 (es)
PT (1) PT4034122T (es)
RS (1) RS67295B1 (es)
SI (1) SI4034122T1 (es)
SM (1) SMT202500493T1 (es)
WO (1) WO2021062264A1 (es)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
KR102789662B1 (ko) 2016-11-29 2025-04-03 피티씨 테라퓨틱스 엠피, 인크. 세피아프테린의 다형체 및 그의 염
WO2018102314A1 (en) 2016-11-29 2018-06-07 Censa Pharmaceuticals Inc. Polymorphic form of sepiapterin
BR112020003865A8 (pt) 2017-09-01 2022-08-16 Censa Pharmaceuticals Inc Composições farmacêuticas compreendendo sepiapterina e seus usos
WO2019232130A1 (en) 2018-05-30 2019-12-05 Censa Pharmaceuticals Inc. Methods for increasing sepiapterin plasma exposure
WO2019232126A1 (en) * 2018-05-30 2019-12-05 Censa Pharmaceuticals Inc. Compositions and methods for increasing tetrahydrobiopterin plasma exposure

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5910304A (en) 1982-12-13 1999-06-08 Texas A&M University System Low-dose oral administration of interferons
CA1320905C (en) 1986-11-06 1993-08-03 Joseph M. Cummins Treatment of immuno-resistant disease
US6036949A (en) 1998-03-05 2000-03-14 Amarillo Biosciences, Inc. Treatment of fibromyalgia with low doses of interferon
SI2926805T1 (sl) * 2014-03-31 2016-09-30 Vasopharm Gmbh Trdni farmacevtski sestavki, obsegajoči biopterinske derivate in uporabe takšnih sestavkov
KR102789662B1 (ko) 2016-11-29 2025-04-03 피티씨 테라퓨틱스 엠피, 인크. 세피아프테린의 다형체 및 그의 염
WO2018102314A1 (en) 2016-11-29 2018-06-07 Censa Pharmaceuticals Inc. Polymorphic form of sepiapterin
BR112020003865A8 (pt) * 2017-09-01 2022-08-16 Censa Pharmaceuticals Inc Composições farmacêuticas compreendendo sepiapterina e seus usos
WO2019232120A1 (en) 2018-05-30 2019-12-05 Censa Pharmaceuticals Inc. Pharmaceutically acceptable salts of sepiapterin

Also Published As

Publication number Publication date
KR20220070477A (ko) 2022-05-31
SI4034122T1 (sl) 2025-12-31
CN114650825A (zh) 2022-06-21
JP7661315B2 (ja) 2025-04-14
JP2022549834A (ja) 2022-11-29
JP2025111476A (ja) 2025-07-30
ES3041002T3 (en) 2025-11-06
FI4034122T3 (fi) 2025-10-08
HUE073483T2 (hu) 2026-01-28
RS67295B1 (sr) 2025-11-28
BR112022003719A2 (pt) 2022-05-31
JOP20220042A1 (ar) 2023-01-30
PL4034122T3 (pl) 2026-01-26
EP4034122B1 (en) 2025-08-13
IL291565A (en) 2022-05-01
PT4034122T (pt) 2025-09-18
CA3150003A1 (en) 2021-04-01
EP4034122A1 (en) 2022-08-03
HRP20251268T1 (hr) 2025-12-05
AU2020353676A1 (en) 2022-04-14
US20220362249A1 (en) 2022-11-17
LT4034122T (lt) 2025-11-10
SMT202500493T1 (it) 2026-01-12
DK4034122T3 (da) 2025-09-15
WO2021062264A1 (en) 2021-04-01

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