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Application filed by Alnylam Pharmaceuticals Inc, Icahn School Med Mount SinaifiledCriticalAlnylam Pharmaceuticals Inc
Priority claimed from PCT/US2014/059160external-prioritypatent/WO2015051318A1/fr
Publication of MA39000A1publicationCriticalpatent/MA39000A1/fr
Publication of MA39000B1publicationCriticalpatent/MA39000B1/fr
108090000623proteins and genesProteins0.000abstract2
229920002477rna polymerPolymers0.000abstract1
230000008685targetingEffects0.000abstract1
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Pharmaceuticals Containing Other Organic And Inorganic Compounds
(AREA)
Saccharide Compounds
(AREA)
Abstract
La présente invention concerne des compositions d'acide ribonucléique double brin (arndb) ciblant le gène alas1, ainsi que des méthodes d'utilisation desdites compositions d'arndb pour altérer (par exemple, inhiber) l'expression du gène alas1.
MA39000A2013-10-042014-10-03Compositions et méthodes permettant d'inhiber l'expression du gène alas1
MA39000B1
(fr)