[go: up one dir, main page]

WO2019037052A1 - Arnsh pour le silençage ciblé de wucam - Google Patents

Arnsh pour le silençage ciblé de wucam Download PDF

Info

Publication number
WO2019037052A1
WO2019037052A1 PCT/CN2017/098909 CN2017098909W WO2019037052A1 WO 2019037052 A1 WO2019037052 A1 WO 2019037052A1 CN 2017098909 W CN2017098909 W CN 2017098909W WO 2019037052 A1 WO2019037052 A1 WO 2019037052A1
Authority
WO
WIPO (PCT)
Prior art keywords
wucam
shrna
vector
cells
psuper
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Ceased
Application number
PCT/CN2017/098909
Other languages
English (en)
Chinese (zh)
Inventor
毛吉炎
Current Assignee (The listed assignees may be inaccurate. Google has not performed a legal analysis and makes no representation or warranty as to the accuracy of the list.)
Shenzhen Biocan Technologies Co ltd
Original Assignee
Shenzhen Biocan Technologies Co ltd
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Shenzhen Biocan Technologies Co ltd filed Critical Shenzhen Biocan Technologies Co ltd
Priority to PCT/CN2017/098909 priority Critical patent/WO2019037052A1/fr
Publication of WO2019037052A1 publication Critical patent/WO2019037052A1/fr
Anticipated expiration legal-status Critical
Ceased legal-status Critical Current

Links

Classifications

    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N15/00Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09Recombinant DNA-technology
    • C12N15/11DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
    • C12N15/113Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing

Definitions

  • the present invention belongs to the field of DNA recombination technology in bioengineering, and specifically relates to shRNA which specifically silences the target protein W UCAM.
  • WUCAM is a newly discovered membrane protein molecule composed of immunoglobulin variable region (IgV), transmembrane region and immunoreceptor tyrosine-based inhibitor motif (ITIM). Expressed on Treg cells, memory T cells, activating T cells, and NK cell surfaces. The study found that: 1) WUCAM is highly constitutively expressed on Treg, and its expression is further up-regulated after activation, which is lowly expressed on memory T cells, while naive CD4+ CD25-T
  • IgV immunoglobulin variable region
  • ITIM immunoreceptor tyrosine-based inhibitor motif
  • WUCAM-Fc fusion protein can promote DC secretion of IL-10 and reduce pro-inflammatory factor IL-12; 3) The ability of WUCAM-Fc fusion protein-treated mature DC to stimulate T cell proliferation is weakened , related to DC secretion of IL-10; 4) in vivo use of WUCAM protein can significantly reduce delayed hypersensitivity, its effect and CTLA-4
  • WUCAM is an important immunomodulator and functions similarly to sputum, which inhibits the cytotoxicity of NK cells and the proliferation of CD4+ T cells and the production of cytokines.
  • WUCAM is a substance that inhibits the action of T cells, and plays a role in inhibiting the excessive activation of T cells under normal conditions; however, this property also makes it easy to be utilized by tumor cells to achieve immune escape. Therefore, WU CAM is a potential target for tumor therapy and requires in-depth research. However, the lack of lentiviral vectors that specifically inhibit the expression of WUCAM gene in the prior art makes the research difficult to develop.
  • the object of the present invention is to synthesize a specific base sequence capable of targeting silent WUCAM, and provide an effective means for further research on the role of WUCAM.
  • the main construct required in the present invention is a silencing vector of WUCAM.
  • the construction of the core silencing vector is divided into two major steps. The first step is to design a 19 bp shRNA core fragment based on the human WUCAM sequence.
  • the synthesized fragment has appropriate restriction sites at both ends, and the target fragment is ligated to the pSUPER vector to form
  • the core silencing vector after transformation, pick positive clones for PCR identification. The correct vector was identified, DNA sequencing was performed, and silencing efficiency was subsequently detected by immunoblotting.
  • a 19 bp shRNA core fragment capable of targeting human WUCAM was designed and synthesized, and its sequence 'J is 5,-GGACGTACACTGGGAGAAT-3, (SEQ ID No: l).
  • Construction of an expression vector that specifically silences WUCAM includes the following steps:
  • the sequence of WUCAM is specifically identified based on the human WUCAM gene sequence using the corresponding software design.
  • the second step the artificial synthesis of double-stranded shRNA fragments
  • the linearized vector is recovered by using a recovery kit, and the recovered fragment is ligated with the shRNA fragment obtained by annealing, transformed, and the positive clone is identified, and the successfully constructed silencing vector is obtained by sequencing.
  • the plasmid was extracted, and the total RNA was extracted after transfecting the cells. After reverse transcription into cDNA, the silencing efficiency was detected by quantitative PCR.
  • the shRNA fragment synthesized in the present invention can specifically silence WUCAM.
  • the experimental results show that the successful construction of the vector can specifically silence the WUCAM and reduce the expression of intracellular WUCAM. Therefore, the application of WUCAM silencing vector can study the function of WUCAM more elaborately and provide a theoretical basis for explaining related mechanisms.
  • DRAWINGS 1 is a schematic diagram showing the results of quantitative PCR detection of WUCAM gene expression of Jurkat cells after transfection of pSUPER-WUCAM vector.
  • Jurkat cells were purchased from the Cell Resource Center of the Shanghai Institute of Biological Sciences, and the RNeasy Mini Kit was purchased from Qiagen.
  • the complete medium described below is a cell culture medium supplemented with 10% fetal bovine serum.
  • a 59 bp sequence was designed in the form of Bgl II-GN18-TT-loop-81NC-Hind III, 81NC is the reverse complement of NG18, the Bgl II cleavage site at the 5' end and the Hind III cleavage site at the 3' end. Point, the obtained sequences are respectively SEQ ID NO:
  • the synthesized shRNA oligonucleotides are mixed in equal amounts in a single strand and annealed to form a double-stranded shRNA. Take 2 g
  • the pSUPER vector, Bgl II and Hind III were digested, electrophoresed, and the linear pSUPER large fragment was recovered. Dilute the linearized pSUPER concentration to 100
  • Ng/ ⁇ , and the double-stranded shRNA obtained by annealing were ligated overnight at 4 °C with T4 DNA ligase (NEB).
  • the ligation product was transformed into ToplO competent cells and plated on LB plates with Kan resistance. Monoclonal shakes were picked on the transformation plates and cultured overnight before being sent to Shanghai Biotech for sequencing. The correct bacteria were sequenced for the extraction of endotoxin-free plasmids, and the pSUPER-WUCAM vector was obtained.
  • Example 3 The pSUPER-WUCAM vector transduced Jurkat cells.
  • Jurkat cells were cultured, and cells grown in good condition were inoculated into a six-well plate at 10 6 cells per well, and the cell density was about 60% after 18 h, using Lipofectamin.
  • the extracted pSUPER-WUCAM vector 3 g was transduced into Jurkat cells. After 6 h, the medium was changed to fresh complete medium and cultured for 48 h.
  • Example 4 Detection of WUCAM gene expression level
  • Jurkat cells and Jurkat cells transduced with pSUPER-WUCAM vector were separately inoculated into 6-well plates. Cell density reaches ⁇ , with RNeasy Mini
  • Kit extracts total RNA from each group of cells, using PrimeScrip RT reagent
  • the shRNA fragment synthesized in the present invention can specifically silence WUCAM.
  • the experimental results show that the successful construction of the vector can specifically silence the WUCAM and reduce the expression of intracellular WUCAM. Therefore, the application of WUCAM silencing vector can study the function of WUCAM more elaborately and provide a theoretical basis for explaining related mechanisms.

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Engineering & Computer Science (AREA)
  • Genetics & Genomics (AREA)
  • Biomedical Technology (AREA)
  • Chemical & Material Sciences (AREA)
  • Molecular Biology (AREA)
  • Organic Chemistry (AREA)
  • Biotechnology (AREA)
  • General Engineering & Computer Science (AREA)
  • Zoology (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Wood Science & Technology (AREA)
  • Microbiology (AREA)
  • Plant Pathology (AREA)
  • Physics & Mathematics (AREA)
  • Biochemistry (AREA)
  • General Health & Medical Sciences (AREA)
  • Biophysics (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)

Abstract

L'invention concerne un ARNsh pour le silençage ciblé d'un gène WUCAM humain.
PCT/CN2017/098909 2017-08-24 2017-08-24 Arnsh pour le silençage ciblé de wucam Ceased WO2019037052A1 (fr)

Priority Applications (1)

Application Number Priority Date Filing Date Title
PCT/CN2017/098909 WO2019037052A1 (fr) 2017-08-24 2017-08-24 Arnsh pour le silençage ciblé de wucam

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
PCT/CN2017/098909 WO2019037052A1 (fr) 2017-08-24 2017-08-24 Arnsh pour le silençage ciblé de wucam

Publications (1)

Publication Number Publication Date
WO2019037052A1 true WO2019037052A1 (fr) 2019-02-28

Family

ID=65438347

Family Applications (1)

Application Number Title Priority Date Filing Date
PCT/CN2017/098909 Ceased WO2019037052A1 (fr) 2017-08-24 2017-08-24 Arnsh pour le silençage ciblé de wucam

Country Status (1)

Country Link
WO (1) WO2019037052A1 (fr)

Citations (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2017048824A1 (fr) * 2015-09-14 2017-03-23 Compass Therapeutics Llc Compositions et procédés de traitement du cancer par antagonisme de la voie cd155/tighit et de tgf-ss

Patent Citations (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2017048824A1 (fr) * 2015-09-14 2017-03-23 Compass Therapeutics Llc Compositions et procédés de traitement du cancer par antagonisme de la voie cd155/tighit et de tgf-ss

Non-Patent Citations (2)

* Cited by examiner, † Cited by third party
Title
DATABASE Nucleotide NCBI; 6 June 2016 (2016-06-06), XP055578701, Database accession no. XM_011512538 *
ZHANG, TAO ET AL.: "Increased Expression of TIGIT on CD4+ T Cells Ameliorates Immune-Mediated Bone Marrow Failure of Aplastic Anemia", JOURNAL OF CELLULAR BIOCHEMISTRY, vol. 115, no. 11, 10 September 2014 (2014-09-10), pages 1918 - 1927, XP055215805, ISSN: 1097-4644 *

Similar Documents

Publication Publication Date Title
WO2019037052A1 (fr) Arnsh pour le silençage ciblé de wucam
CN109022436A (zh) 特异抑制3β-HSD基因表达的shRNA重组载体构建与应用
WO2019037133A1 (fr) Arnsh ciblant app silencieux
WO2019037057A1 (fr) ARNSH CIBLANT DD1α SILENCIEUX
WO2019036872A1 (fr) Arnsh pour l'inactivation de l'expression d'un gène pta1
WO2017214940A1 (fr) Vecteur d'expression lentiviral pour favoriser spécifiquement l'expression élevée du gène cplx2, et ses applications
WO2019036869A1 (fr) Arnsh du gène tl6 humain et ses applications
WO2019037053A1 (fr) Arn court en épingle à cheveux du gène aitr humain et applications correspondantes
WO2018170764A1 (fr) Vecteur pour arni et son application
WO2018170762A1 (fr) Vecteur d'expression d'arni du gène tnlg5a, procédé de construction associé et application correspondante
CN110964727A (zh) 特异抑制c-myc基因表达的shRNA慢病毒表达载体构建方法与应用
WO2019037130A1 (fr) Arnsh du gène ampar humain et application associée
WO2019037049A1 (fr) Arnsh du gène erbb2 humain et applications
WO2019000148A1 (fr) Arnsi du gène abcb6 humain et utilisation correspondante
WO2017214828A1 (fr) Vecteur d'expression lentiviral pour favoriser spécifiquement l'expression élevée du gène prkcz, et ses applications
WO2019037055A1 (fr) Arnsh du gène grd4 humain et application d'arnsh
WO2018170765A1 (fr) Vecteur d'interférence arn du gène imd16 et son application
WO2019037048A1 (fr) Vecteur lentiviral à haute expression de gène de l'indoléamine 2,3-dioxygénase, lentivirus, et sa méthode de construction
WO2017214944A1 (fr) Vecteur lentiviral pour favoriser l'expression supérieure de gènes tigit et ses applications
WO2017214945A1 (fr) Vecteur d'expression lentiviral pour améliorer le taux d'expression du gène de l'hepcidine, et ses applications
WO2017214833A1 (fr) Vecteur lentiviral pour favoriser spécifiquement l'expression élevée du gène erbb2, et ses applications
WO2019036868A1 (fr) Vecteur lentiviral de surexpression de gène atténuateur des lymphocytes b/t, lentivirus, et procédé de construction associé
WO2017214910A1 (fr) Vecteur d'expression lentiviral pour favoriser spécifiquement l'expression élevée du gène tβ4, et ses applications
CN118703565A (zh) Ltf基因过表达的山羊乳腺上皮细胞的构建方法及应用
WO2017214831A1 (fr) Vecteur lentiviral pour favoriser spécifiquement l'expression élevée du gène nrg1, et ses applications

Legal Events

Date Code Title Description
121 Ep: the epo has been informed by wipo that ep was designated in this application

Ref document number: 17922227

Country of ref document: EP

Kind code of ref document: A1

NENP Non-entry into the national phase

Ref country code: DE

122 Ep: pct application non-entry in european phase

Ref document number: 17922227

Country of ref document: EP

Kind code of ref document: A1