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Application filed by Alnylam Pharmaceuticals IncfiledCriticalAlnylam Pharmaceuticals Inc
Publication of AR110225A1publicationCriticalpatent/AR110225A1/es
230000009368gene silencing by RNAEffects0.000abstract3
201000010099diseaseDiseases0.000abstract1
208000037265diseases, disorders, signs and symptomsDiseases0.000abstract1
208000019423liver diseaseDiseases0.000abstract1
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Pharmaceuticals Containing Other Organic And Inorganic Compounds
(AREA)
Abstract
Agentes de ARNi, por ejemplo, agentes de ARNi de hebra doble, direccionados al gen de Serpina1 y métodos para usar dichos agentes de ARNi para inhibir la expresión de Serpina1 y métodos de tratamiento de sujetos que padecen una enfermedad asociada con Serpina1, tal como un trastorno hepático.
ARP170103272A2016-11-232017-11-23COMPOSICIONES DE ARNi DE SERPINA1 Y SUS MÉTODOS DE USO
AR110225A1
(es)