MY205057A - Varian aav and compositions, methods and uses for gene transfer to cells, organs and tissues - Google Patents
Varian aav and compositions, methods and uses for gene transfer to cells, organs and tissuesInfo
- Publication number
- MY205057A MY205057A MYPI2019002961A MYPI2019002961A MY205057A MY 205057 A MY205057 A MY 205057A MY PI2019002961 A MYPI2019002961 A MY PI2019002961A MY PI2019002961 A MYPI2019002961 A MY PI2019002961A MY 205057 A MY205057 A MY 205057A
- Authority
- MY
- Malaysia
- Prior art keywords
- aav
- organs
- tissues
- cells
- gene transfer
- Prior art date
Links
- 108090000623 proteins and genes Proteins 0.000 title abstract 4
- 238000000034 method Methods 0.000 title abstract 2
- 210000000056 organ Anatomy 0.000 title abstract 2
- 239000000203 mixture Substances 0.000 title 1
- 239000013607 AAV vector Substances 0.000 abstract 3
- 102000040430 polynucleotide Human genes 0.000 abstract 2
- 108091033319 polynucleotide Proteins 0.000 abstract 2
- 239000002157 polynucleotide Substances 0.000 abstract 2
- 241000702421 Dependoparvovirus Species 0.000 abstract 1
- 230000002401 inhibitory effect Effects 0.000 abstract 1
- 230000001404 mediated effect Effects 0.000 abstract 1
- 150000007523 nucleic acids Chemical group 0.000 abstract 1
- 102000004196 processed proteins & peptides Human genes 0.000 abstract 1
- 108090000765 processed proteins & peptides Proteins 0.000 abstract 1
- 102000004169 proteins and genes Human genes 0.000 abstract 1
- 230000001225 therapeutic effect Effects 0.000 abstract 1
- 238000013518 transcription Methods 0.000 abstract 1
- 230000035897 transcription Effects 0.000 abstract 1
Landscapes
- Medicines Containing Material From Animals Or Micro-Organisms (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
Abstract
The invention relates to adeno-associated virus (AAV) serotype AAV-Rh74 and related AAV vectors, and AAV-Rh74 and related AAV vector mediated gene transfer methods and uses. In particular, AAV-Rh74 and related AAV vectors target polynucleotides to cells, tissues or organs for expression (transcription) of genes encoding therapeutic proteins and peptides, and polynucleotides that function as or are transcribed into inhibitory nucleic acid sequences. (Figure 6)
Applications Claiming Priority (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201361857161P | 2013-07-22 | 2013-07-22 |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| MY205057A true MY205057A (en) | 2024-09-30 |
Family
ID=94969615
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| MYPI2019002961A MY205057A (en) | 2013-07-22 | 2014-07-22 | Varian aav and compositions, methods and uses for gene transfer to cells, organs and tissues |
Country Status (1)
| Country | Link |
|---|---|
| MY (1) | MY205057A (en) |
-
2014
- 2014-07-22 MY MYPI2019002961A patent/MY205057A/en unknown
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