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MY205057A - Varian aav and compositions, methods and uses for gene transfer to cells, organs and tissues - Google Patents

Varian aav and compositions, methods and uses for gene transfer to cells, organs and tissues

Info

Publication number
MY205057A
MY205057A MYPI2019002961A MYPI2019002961A MY205057A MY 205057 A MY205057 A MY 205057A MY PI2019002961 A MYPI2019002961 A MY PI2019002961A MY PI2019002961 A MYPI2019002961 A MY PI2019002961A MY 205057 A MY205057 A MY 205057A
Authority
MY
Malaysia
Prior art keywords
aav
organs
tissues
cells
gene transfer
Prior art date
Application number
MYPI2019002961A
Inventor
A High Katherine
N Yazicioglu Mustafa
Anguela Xavier
Original Assignee
Childrens Hospital Philadelphia
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Childrens Hospital Philadelphia filed Critical Childrens Hospital Philadelphia
Publication of MY205057A publication Critical patent/MY205057A/en

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  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)

Abstract

The invention relates to adeno-associated virus (AAV) serotype AAV-Rh74 and related AAV vectors, and AAV-Rh74 and related AAV vector mediated gene transfer methods and uses. In particular, AAV-Rh74 and related AAV vectors target polynucleotides to cells, tissues or organs for expression (transcription) of genes encoding therapeutic proteins and peptides, and polynucleotides that function as or are transcribed into inhibitory nucleic acid sequences. (Figure 6)
MYPI2019002961A 2013-07-22 2014-07-22 Varian aav and compositions, methods and uses for gene transfer to cells, organs and tissues MY205057A (en)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
US201361857161P 2013-07-22 2013-07-22

Publications (1)

Publication Number Publication Date
MY205057A true MY205057A (en) 2024-09-30

Family

ID=94969615

Family Applications (1)

Application Number Title Priority Date Filing Date
MYPI2019002961A MY205057A (en) 2013-07-22 2014-07-22 Varian aav and compositions, methods and uses for gene transfer to cells, organs and tissues

Country Status (1)

Country Link
MY (1) MY205057A (en)

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