[go: up one dir, main page]

HK1218138B - Exon skipping compositions for treating muscular dystrophy - Google Patents

Exon skipping compositions for treating muscular dystrophy Download PDF

Info

Publication number
HK1218138B
HK1218138B HK16106036.5A HK16106036A HK1218138B HK 1218138 B HK1218138 B HK 1218138B HK 16106036 A HK16106036 A HK 16106036A HK 1218138 B HK1218138 B HK 1218138B
Authority
HK
Hong Kong
Prior art keywords
antisense
dystrophin
exon
oligomer
oligomers
Prior art date
Application number
HK16106036.5A
Other languages
English (en)
French (fr)
Chinese (zh)
Other versions
HK1218138A1 (en
Inventor
K. Bestwick Richard
Elizabeth Frank Diane
Original Assignee
Sarepta Therapeutics, Inc.
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Sarepta Therapeutics, Inc. filed Critical Sarepta Therapeutics, Inc.
Priority claimed from PCT/US2014/029766 external-priority patent/WO2014153240A2/en
Publication of HK1218138A1 publication Critical patent/HK1218138A1/en
Publication of HK1218138B publication Critical patent/HK1218138B/en

Links

Claims (3)

  1. Antisense-Oligonukleotid mit der folgenden Struktur: wobei und wobei ^ = die Stereochemie des Phosphor-Zentrums nicht definiert ist; oder ein pharmazeutisch unbedenkliches Salz davon.
  2. Pharmazeutische Zusammensetzung, umfassend das Antisense-Oligonukleotid nach Anspruch 1 und einen pharmazeutisch unbedenklichen Träger.
  3. Zusammensetzung nach Anspruch 2 zur Verwendung bei der Behandlung von Duchenne-Muskeldystrophie.
HK16106036.5A 2013-03-14 2014-03-14 Exon skipping compositions for treating muscular dystrophy HK1218138B (en)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201361782706P 2013-03-14 2013-03-14
US201361782706P 2013-03-14
PCT/US2014/029766 WO2014153240A2 (en) 2013-03-14 2014-03-14 Exon skipping compositions for treating muscular dystrophy

Publications (2)

Publication Number Publication Date
HK1218138A1 HK1218138A1 (en) 2017-02-03
HK1218138B true HK1218138B (en) 2019-10-04

Family

ID=

Similar Documents

Publication Publication Date Title
AU2022202393B2 (en) Exon skipping compositions for treating muscular dystrophy
US20220364093A1 (en) Exon skipping compositions for treating muscular dystrophy
US20150361428A1 (en) Exon skipping compositions for treating muscular dystrophy
HK40074954A (en) Exon skipping compositions for treating muscular dystrophy
HK40008691A (en) Exon skipping compositions for treating muscular dystrophy
HK1218138B (en) Exon skipping compositions for treating muscular dystrophy
HK1219755B (en) Exon skipping compositions for treating muscular dystrophy